Group

Case

Age (years)

Tumor Type

Past SU

Past CH

Past RT

Tumor cross-section area (cm2)

Best Response to Treatment

OS

(months)

PFS

(months)

Baseline

Best response

Brainstem glioma

19

2

Pilocytic astrocytoma

/midbrain

Yes

No

No

19.0

resolved

CR

94.2+

19.0

24

4

DIPG

No

No

Yes

0.36

resolved

CR

14.2

14.2

26

6

DIPG

No

No

Yes

3.90

resolved

PR

8.7

8.5

Low-grade glioma

11

8

Ganglio-

Glioma

(MC, L)

Yes

No

No

4.56

1.08

PR

189.7+

189.7+

32

0.83

Ganglio-

glioma-

desmoplastic infantile

Yes

No

No

18.0

4.2

PR

36.6+

36.6+

34

9

Pilocytic astrocytoma

(MC, D, L)

Yes

Yes

No

4.33

1.26

PR

39.0+

15.4