| MTT | Exondys 51 |
| 1. 100% dystrophin production | 0.28% dystrophin m-RNA increase |
| 2. 70% muscle fiber increase and histology improved | None |
| 3. 123% strength increase in 18 months | None |
| 4. 48.7% decrease in serum CPK in 1 year | None |
| 5. 19% increase in breathing capacity | None |
| 6. Physical capacity improved | None |
| 7. Life prolonged | None |
| 8. For DMD, BMD and other MDs | For 13% DMD with Exon 51 skipping |