Substance | Subject | Benefit | Adverse Effects Observed | Drawbacks |
AAV9-ADAR2 injection | Mice | ・ Rescue of motor neurons from death ・ Neuron regeneration | N/A | ・ Little known mechanism |
Riluzole | Humans | ・ Prolong overall survival?/delay disease progression | ・ Diarrhea ・ Dizziness ・ Fatigue ・ Nausea |
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Stem cells (Human Umbilical Cord Blood Cells, HUCBCs) | Mice | ・ Low immunogenicity ・ Retard disease progression ・ Prolong survival ・ Improve motor function and neuromuscular transmission ・ attenuate astrogliosis | N/A | ・ Ethical issue with use |