TRIAL N.

STATUS

N. PATIENT

CONDITION

COMPOUND

FUNCTION

PHASE

NCT03395704

Completed

70

Haemocromatosis

LJPC-401

Synthetic human hepcidin

Phase II

NCT03381833

Terminated

84

Beta-Thalassemia

LJPC-401

Sintetic human hepcidin

Phase II

NCT04057040

Active not recruiting

80

Policitemia vera

PTG 300

Hepcidin mimetic

Phase II

NCT06033586

Not yet recruiting

50

Policitemia vera

PTG 300

Hepcidin mimetic

PhaseIII

NCT04767802

Active, not recruiting

20

Policitemia vera

PTG 300

Hepcidin mimetic

Phase II

NCT04054921

Completed

34

β-thalassemia

Ineffective Erythropoiesis

PTG300

Hepcidin mimetic

Phase II

NCT05210790

Recruiting

250

Policitemia vera

PTG 300

Hepcidin mimetic

Phase III

NCT02340572

Completed

48

Healthy

PRS-080

Hepcidin blocker

Phase I

NCT03325621

Completed

11

Anemia of Chronic Kidney Disease

PRS-080

Hepcidin blocker

Phase I-II

NCT02754167

Unknown

24

Anemia of Chronic Kidney Disease

PRS-080

Hepcidin blocker

Phase I-II

NCT05499013

Recruiting

65

Policitemia Vera

SLN124

Anti TMPRSS 6

Phase I-II

NCT03165864

Completed

36

Thalassemia

IONIS TMPRSS6-Lrx

Anti TMPRSS 6

Phase I

NCT05077436

Completed

28

Healthy

Vamifeport

AntiFPN

Phase I

NCT04817670

Recruiting

24

Sickle Cell Disease

Vamifeport

(VIT 2763)

Anti FPN

Phase II

NCT04364269

Completed

25

Beta-Thalassemia

Vamifeport

(VIT 2763)

Anti FPN

Phase II

NCT04938635

Withdrawn

0

Beta-Thalassemia

Vamifeport

(VIT 2763)

AntiFPN

Phase II

NCT04707261

(ADIDAS)

Recruiting

1990

Anemia

Heart Failure

Dapaglifozin

Reduction hepcidin

pathwhay

Phase IV